News & Events
July 21, 2021
WEBINAR | How RDCA-DAP Can Help Inform Optimal Trial Design in Progressive Rare Disease
When: July 21, 2021, 12 p.m. ET
Case Study: Northstar Ambulatory Assessment as an outcome assessment in Duchenne muscular dystrophy
Presenters: Varun Aggarwal, PhD, Director, Statistical and Mathematical Medicine, Quantitative Medicine; Kevin Krudys, PhD, Office of Clinical Pharmacology, FDA
RDCA-DAP team: Jeff Barrett, PhD, FCP, Senior Vice President, RDCA-DAP Lead; Alexandre Bétourné, PhD, PharmD, Scientific Director, RDCA-DAP
June 15, 2021 - June 16, 2021
Design of Clinical Trials in New-Onset Type 1 Diabetes: Regulatory Considerations for Drug DevelopmentCritical Path Institute invites you to the upcoming free virtual workshop, Design of Clinical Trials in New-Onset Type 1 Diabetes: Regulatory Considerations for Drug Development, June 15-16, 2021. The purpose of this scientific workshop is to discuss the existing evidence regarding the role of C-peptide in clinical trials intended to support regulatory decision making, unique regulatory considerations......
June 14, 2021
Register Now | RDCA-DAP Webinar Series: Value of Integrated Data and Analytics in Rare Disease Drug Development
When: June 16, 2021, 12 p.m. ET
Case Study: Modeling disease progression in polycystic kidney disease to inform trial design
Presenters: Rhoda Muse, PhD, Scientist 1, Quantitative Medicine; Klaus Romero, MD, MS, FCP, Chief Science Officer and Executive Director of Clinical Pharmacology; Jackson Burton, PhD, Executive Director, Quantitative Medicine
RDCA-DAP Team: Jeff Barrett, PhD, FCP., Senior Vice President, RDCA-DAP Lead; Alexandre Bétourné, PhD, PharmD, Scientific Director, RDCA-DAP
May 26, 2021
PSTC 15-year Anniversary Webinar SeriesJoin scientists from PSTC member companies, health authorities and other key opinion leaders during the PSTC 15-year Anniversary Webinar Series where they will share information about collaborative cutting-edge science taking place within the consortium’s working groups and engage in discussion on the complexities and opportunities surrounding safety biomarkers and biomarker qualification. Each webinar in the......
May 19, 2021 - May 20, 2021
2021 PKD Regulatory Summit | May 19-20
Join C-Path’s PKDOC and The PKD Foundation for the 2021 PKD Regulatory Summit on May 19 and 20. Together with key stakeholders from around the world, the consortium will address current unmet drug development needs for PKD, identify tools that are needed to deliver new therapies to patients, and catalyze the development of a regulatory framework to enable advancement of new treatments.