April 17, 2025 ACE Inhibitors as a Cardioprotective Treatment in Dystrophinopathies ACE inhibitors were the first pharmacological class shown to benefit heart failure treatment...
March 24, 2025 Lysosomal Storage Disease Data Sharing Workshop, Webinar Series Session #2: Case Studies #1 – Proactive Data Sharing This webinar from Critical Path Institute's Critical Path to Lysosomal Diseases Consortium presents...
February 24, 2025 Lysosomal Storage Disease Data Sharing Workshop, Webinar Series – Session #1: Setting the Scene C-Path's CPLD team presents, "Lysosomal Storage Disease Data Sharing Workshop, Webinar Series - Session #1...
February 20, 2025 Vivli and RDCA-DAP: Data Platform Partnerships to Promote Rare Disease Data Sharing This webinar presentation will be held by C-Path collaborator Julie Wood, Chief Operating Officer at Vivli.
February 20, 2025 Vivli and RDCA-DAP Present: Data Platform Partnerships to promote Rare Disease Data Sharing Join Julie Wood, Chief Operating Officer at Vivli, for an engaging webinar, Thursday, February 20, where she’ll discuss...
January 28, 2025 TRxA Funding Opportunities 2025 On January 28, C-Path’s Translational Therapeutics Accelerator (TRxA)...
January 17, 2025 CP-RND ALS Public-Private Partnership Public Forum A public forum for stakeholders Critical Path Institute's (C-Path) Critical Path for Rare and Neurodegenerative Diseases...
December 12, 2024 The Power of Data Sharing and Collaboration Across LGMDs in a Pre-competitive, Neutral Environment This event featured Dr. Volker Straub, a renowned neuromuscular genetics expert...
November 14, 2024 Advanced in Vitro Modelling of Neuromuscular Diseases and Therapeutics Join this webinar to explore innovative, multidisciplinary approaches in disease modeling, drug testing, and tissue engineering...
October 29, 2024 Webinar: New Findings on Inequities in Rare Diseases: How They Impact Research and Clinical Trials Processes Join us Tuesday, October 29, at noon Eastern for an important webinar, New Findings on Inequities in Rare Diseases...