C-Path Opens Access to Duchenne Regulatory Science Consortium Database Database will allow sharing of individual-level data with the goal of accelerating therapy development for Duchenne muscular dystr
Data Collaboration Center Request for Proposal RFP: The RDCA Branding & Web Portal Data Collaboration Center’s (DCC’s) platform development team is seeking a proposal, i
May 19, 2021-May 20, 2021 View Now | 2021 PKD Regulatory Summit | May 19-20 The Critical Path Institute’s Polycystic Kidney Disease Outcomes Consortium (PKDOC), The PKD Foundation and Otsuka invite you vi
April 14, 2021-April 15, 2021 Identifying COAs for Use in Rare Disease Treatment Trials Presented at the PRO Consortium 2021 Workshop, held virtually April 14-15, 2021:
CPTA Welcomes Triplet Therapeutics Chief Medical Officer as Industry Co-Director C-Path’s Critical Path to Therapeutics for the Ataxias Consortium is pleased to announce the appointment of Irina Antonijevi
C-Path’s Alzheimer’s Disease Consortium Expands Data Repository New patient-level data will facilitate more efficient clinical trial design TUCSON, Ariz., April 12, 2021 — The Critical Path In
CP-SCD Announces Pfizer Executive as its First Industry Co-Director C-Path’s Critical Path to Sickle Cell Disease Consortium (CP-SCD) is pleased to announce Dr. David Readett of Pfizer as its firs
May 7, 2021 COVID-19 Mitigation Strategies in Pediatric Rare Disease Clinical Trials Virtual Workshop COVID-19 Mitigation Strategies in Pediatric Rare Disease Clinical Trials Virtual Workshop Friday May 7, 2021 12:00 – 1:30 pm Ea
April 7, 2021 FAIR data sharing: The roles of common data elements and harmonization. Journal of Biomedical Informatics. 2020 July D. Kush, D. Warzel, M.A. Kush, A. Sherman, E.A. Navarro, R. Fitzmartin, F. Pétavy, J. Galvez, L.B. Becnel, F.L. Zhou, N. Harmon..
April 7, 2021 Standardized Data Structures in Rare Diseases: CDISC User Guides for Duchenne Muscular Dystrophy and Huntington’s Disease Interest in drug development for rare diseases has expanded dramatically since the Orphan Drug Act was passed in 1983,