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Pediatrics
Critical Path for Alpha-1 Antitrypsin Deficiency
Rare and Orphan Diseases
Pediatrics
Critical Path for Lysosomal Diseases Pre-Consortium
Rare and Orphan Diseases
Pediatrics
Duchenne Regulatory Science Consortium
Neuroscience
Rare and Orphan Diseases
Pediatrics
International Neonatal Consortium
Pediatrics
Polycystic Kidney Disease Outcomes Consortium
Rare and Orphan Diseases
Pediatrics
Rare Disease Clinical Outcome Assessment Consortium
Core Competencies
Rare and Orphan Diseases
Pediatrics
Clinical Outcome Assessment
Type 1 Diabetes Consortium
Pediatrics