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February 1, 2025

Accelerating Parkinson’s Disease Drug Development with Federated Learning Approaches

Parkinson’s Disease is a progressive neurodegenerative disorder afflicting almost 12 million people...

February 13, 2025

Pediatric drug development faces signiﬁcant challenges, including underfunding, ethical concerns, and complex regulatory...

February 1, 2025

Healthcare datasets can be used for many different purposes in the pursuit of...

January 7, 2025

The value of involving people living with diseases in the research process is increasingly recognized...

December 13, 2024

In the rapidly evolving landscape of healthcare and drug development, the ability to efficiently collect...

November 27, 2024

Autosomal Recessive Polycystic Kidney Disease (ARPKD) is a rare genetic disease. It occurs in about one in 20,000 births...

November 27, 2024

The mission of the Polycystic Kidney Disease Foundation is to fund research, advocate for patients, and ultimately to end PKD..

December 12, 2024

Item response theory (IRT) models are an increasingly popular method choice for...

November 27, 2024

Duchenne muscular dystrophy (DMD), a rare pediatric disease, presents numerous challenges when designing clinical trials...

December 1, 2024

Naomi Knoble, and Lindsey T. Murray on behalf of the Rare Disease Clinical Outcome Assessment Consortium. View all authors and aff