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August 1, 2021

A Disease Progression Model to Quantify the Nonmotor Symptoms of Parkinson’s Disease in Participants With Leucine-Rich Repeat Kinase 2 Mutation

Ahamadi M, Mehrotra N, Hanan N, Lai Yee K, Gheyas F, Anton J, Bani M, Boroojerdi B, Smit H, Weidemann J, Macha S, Thuillier V...

July 8, 2021

Digital Progression Biomarkers as Novel Endpoints in Clinical Trials: A Multistakeholder Perspective

Stephenson D, Badawy R, Mathur S, Tome M, Rochester L. Digital Progression Biomarkers as Novel Endpoints in Clinical Trials...

May 20, 2021

The Role of Patient-reported Outcomes and Medication Adherence Assessment in Patient-focused Drug Development for Solid Organ Transplantation

April 7, 2021

FAIR data sharing: The roles of common data elements and harmonization. Journal of Biomedical Informatics. 2020 July

D. Kush, D. Warzel, M.A. Kush, A. Sherman, E.A. Navarro, R. Fitzmartin, F. Pétavy, J. Galvez, L.B. Becnel, F.L. Zhou, N. Harmon..

April 7, 2021

Standardized Data Structures in Rare Diseases: CDISC User Guides for Duchenne Muscular Dystrophy and Huntington’s Disease

Interest in drug development for rare diseases has expanded dramatically since the Orphan Drug Act was passed in 1983,

March 20, 2021

Current state of cardiac troponin testing in Duchenne muscular dystrophy cardiomyopathy: review and recommendations from the Parent Project Muscular Dystrophy expert panel

March 19, 2021

Qualification of translational safety biomarkers

March 8, 2021

CORRECTION: Evaluation of Multiple Sclerosis Disability Outcome Measures Using Pooled Clinical Trial Data

January 19, 2021

The Utility of Novel Urinary Biomarkers in Mice for Drug Development Studies

January 8, 2021

Effective Data Sharing as a Conduit for Advancing Medical Product Development

Patient-level data sharing has the potential to significantly impact the lives of patients by optimizing and improving the medical

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