June 5, 2026 Public Private Partnerships for Rare Neurodegenerative Disease Critical Path Institute's Critical Path for Rare Neurodegenerative Diseases consortium, will convene partners from the FDA...
April 1, 2026 Advancing Rare Disease Innovation Through Responsible Data Sharing — Key Takeaways from the RISE Together: Data Sharing Across the Rare Disease Ecosystem At a recent public workshop co-convened by the Duke-Margolis Institute for Health Policy...
February 16, 2026 Epilepsy disease classification: a community effort to enhance the Mondo Disease Ontology Epilepsy is a diverse group of neurological disorders affecting over 50 million people worldwide.
February 20, 2026 What Collaboration Makes Possible On a Tuesday afternoon in the fall of 2019, a biostatistician from a pharmaceutical company...
February 12, 2026 Building the Infrastructure of Hope Medical history is usually written as a chronicle of individual breakthroughs. We learn about Fleming discovering penicillin...
May 27, 2025 C-Path Welcomes Avidity Biosciences as Newest Member to Duchenne Consortium C-Path is excited to welcome Avidity Biosciences as a new member of the Duchenne Regulatory Science Consortium...
May 15, 2025 From Awareness to Action: How C-Path’s HD-RSC Is Transforming the Future of Huntington’s Disease May 15, marks Huntington’s Disease Awareness Day, a key moment during Huntington’s Awareness...
May 22, 2025 RDCA-DAP and NORD’s IAMRARE Platform to Platform Federation: Lessons Learned Patient data is a key asset in understanding the progression of rare diseases...
March 24, 2025 Lysosomal Storage Disease Data Sharing Workshop, Webinar Series Session #2: Case Studies #1 – Proactive Data Sharing This webinar from Critical Path Institute's Critical Path to Lysosomal Diseases Consortium presents...
February 26, 2025 Transforming Data into Breakthroughs: 5 Years of RDCA-DAP Journey and Impact In honor of Rare Disease Month, Alexandre Bétourné took some time to sit down and discuss the impact RDCA-DAP has made...
