December 1, 2024 Advancing rare disease measurement through the Rare Disease Clinical Outcome Assessment Consortium Naomi Knoble, and Lindsey T. Murray on behalf of the Rare Disease Clinical Outcome Assessment Consortium. View all...
November 27, 2024 C-Path’s Romero, Swingle Named to 100 Most Innovative and Influential Healthcare Leaders in AZ Big Media C-Path CEO Klaus Romero and President & COO Kristen Swingle, President and COO were recently named to the 100 Most...
November 27, 2024 A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies Duchenne muscular dystrophy (DMD), a rare pediatric disease, presents numerous challenges when designing clinical trials...
November 27, 2024 Autosomal Recessive Polycystic Kidney Disease (ARPKD)Adjunct EL-PFDD Scientific Workshop Report The mission of the Polycystic Kidney Disease Foundation is to fund research, advocate for patients, and ultimately to end PKD..
November 27, 2024 Voice of the Patient report Externally-Led Patient-Focused Drug Development (EL-PFDD) Meeting for ARPKD Patients and their Families Autosomal Recessive Polycystic Kidney Disease (ARPKD) is a rare genetic disease. It occurs in about one in 20,000 births...
November 19, 2024 C-Path’s TRxA Announces $1 Million Award for Drug Development Project in Type 1 Diabetes C-Path today announced that its Translational Therapeutics Accelerator (TRxA) program, in partnership...
November 17, 2024 Advancing Neonatal Drug Development: Celebrating Progress on World Prematurity Day On this occasion of World Prematurity Awareness Day, we reflect on the immense progress we have made together and recognize...
November 14, 2024 C-Path’s Initiative to Optimize Clinical Trial Design in New-Onset Type 1 Diabetes In honor of World Diabetes Day and the need to improve diabetes treatment, Critical Path Institute’s Type 1 Diabetes Consortium
November 14, 2024 Advanced in Vitro Modelling of Neuromuscular Diseases and Therapeutics Join this webinar to explore innovative, multidisciplinary approaches in disease modeling, drug testing, and tissue engineering...
November 13, 2024 C-Path Announces Global Evidence in Medicine for Parkinson’s Disease (GEM‑PD) Initiative C-Path expands its worldwide leadership in accelerating drug development in neurology; seeks additional collaborators to broaden..