Duchenne Regulatory Science Consortium Founded in 2015, D-RSC supports collaborative research through shared data access and advances development of drug development too
Regulatory Science Program The Regualtory Science (RegSci) Program was founded in 2020 to lead regulatory strategy development and supports regulatory submis
Huntington’s Disease Regulatory Science Consortium Critical Path for Alpha-1 Antitrypsin Deficiency CPA-1 is a public-private partnership comprised of industry partners, academic re
Polycystic Kidney Disease Outcomes Consortium Autosomal Dominant Polycystic Kidney Disease (ADPKD) is a debilitating genetic disease affecting more than 600,000 Americans and 1
Predictive Safety Testing Consortium Although companies have developed newer methods to test drug safety, these are not globally accepted by the FDA or EMA as proof of
Rare Disease Clinical Outcome Assessment Consortium The Rare Disease Clinical Outcome Assessment Consortium enables precompetitive, multi-stakeholder collaboration aimed at identifyi
Rare Disease Cures Accelerator-Data and Analytics Platform Additional Resources For additional resources, such as a list of diseases’ data areas housed in the platform, past webinars,
Patient-Centered Evidence Consortium PRO measures assess one or more aspects of a patient’s health status based on information gathered directly from the patient, wi
Electronic Clinical Outcome Assessment Consortium The Electronic Clinical Outcome Assessment (eCOA) Consortium provides scientific leadership and best practice recommendations surr
