January 12, 2025 National Pharmacist Day: Recognizing These Pillars in Healthcare Every year on January 12th, we pause to celebrate National Pharmacist Day — a day dedicated to recognizing the vital role pharma
January 7, 2025 Inclusion in neurological research: empowering people living with neurological diseases Maria Teresa Ferretti, Maria Bonaria Uccheddu, Richelle Flanagan, Iracema Leroi & Elena Moro Nature Reviews Neurology (2025)
December 13, 2024 Real-world evidence in the cloud: Tutorial on developing an end-to-end data and analytics pipeline using Amazon Web Services resources In the rapidly evolving landscape of healthcare and drug development, the ability to efficiently collect...
December 12, 2024 The Power of Data Sharing and Collaboration Across LGMDs in a Pre-competitive, Neutral Environment This event featured Dr. Volker Straub, a renowned neuromuscular genetics expert...
December 12, 2024 Investigating item response theory model performance in the context of evaluating clinical outcome assessments in clinical trials Item response theory (IRT) models are an increasingly popular method choice for...
December 10, 2024 Biomarkers 101: A Patient’s Perspective on the Importance of Identifying New Biomarkers Biomarkers are emerging as powerful tools in the field of kidney health, playing a crucial role in the diagnosis, monitoring...
December 1, 2024 Advancing rare disease measurement through the Rare Disease Clinical Outcome Assessment Consortium Naomi Knoble, and Lindsey T. Murray on behalf of the Rare Disease Clinical Outcome Assessment Consortium. View all authors and aff
November 27, 2024 C-Path’s Romero, Swingle Named to 100 Most Innovative and Influential Healthcare Leaders in AZ Big Media C-Path CEO Klaus Romero and President & COO Kristen Swingle, President and COO were recently named to the 100 Most...
November 27, 2024 A computational tool to optimize clinical trial parameter selection in Duchenne muscular dystrophy: A practical guide and case studies Duchenne muscular dystrophy (DMD), a rare pediatric disease, presents numerous challenges when designing clinical trials...
November 27, 2024 Autosomal Recessive Polycystic Kidney Disease (ARPKD)Adjunct EL-PFDD Scientific Workshop Report The mission of the Polycystic Kidney Disease Foundation is to fund research, advocate for patients, and ultimately to end PKD..
