Breaking Down Barriers in Support of Patients with Rare Diseases


You’re invited to join C-Path’s Gina Calarco Smith at the upcoming Breaking Down Barriers in Support of Rare Diseases webinar. Smith, Scientific Director of Pediatrics at C-Path, will be on a panel of rare disease experts who will break down the latest in drug development, clinical trials, patient advocacy and more. Hosted by Labcorp on Wednesday, February 22, 4 p.m. GMT | 11 a.m. EST, this event is tailored directly for those who work in the rare disease space of scientific research.

There are over 7,000 rare diseases, and one in 10 individuals worldwide have a rare disease. More than 675 diseases have some research and development targeting supportive care, treatment or a cure for these patients, with approximately only 5% of indications having a treatment available. There is tremendous opportunity and an even larger patient need.

Success in this space requires collaboration across many stakeholders including families and patients, sites, investigators, labs, advocacy groups, regulators and the various service providers that support clinical trial delivery. Rapid engagement and work with these stakeholders are important in the search for answers.

This webinar will provide important perspectives from key stakeholders on:

  • The profoundly personal side of rare disease: Humanizing the therapeutic journey of patients
  • Ways to successfully collaborate with patients, families and advocacy groups
  • Supporting patient diagnosis and connectivity to recruitment for clinical trials
  • Ensuring clinical trial data can support regulatory and commercial decisions

Register to learn about breaking down barriers in support of patients with rare diseases.

Register Now