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Critical Path for Sickle Cell Disease
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Critical Path to Therapeutics for the Ataxias
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Duchenne Regulatory Science Consortium
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TB-Platform for Aggregation of Clinical TB Studies
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TTC
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Friedreich’s Ataxia Integrated Clinical Database
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Trial Outcome Markers Initiative in T1D Consortium
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Huntington’s Disease Regulatory Science Consortium
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Translational Therapeutics Accelerator
INC
International Neonatal Consortium
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Coalition for Accelerating Standards & Therapies
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